Gene Therapy

FDA Approves Otarmeni, the First Gene Therapy for Genetic Hearing Loss

The U.S. FDA has approved Otarmeni (lunsotogene parvec-cwha), Regeneron Pharmaceuticals’ gene therapy for severe-to-profound sensorineural hearing loss caused by biallelic OTOF gene variants. Otarmeni is the first approved gene therapy for genetic hearing loss and the first dual-AAV vector-based gene therapy to reach approval. The decision is notable not only for rare disease innovation, but […]

Medical Industry News

UCB to Acquire Neurona Therapeutics to Expand Regenerative Medicine in Epilepsy

UCB has announced an agreement to acquire U.S.-based Neurona Therapeutics for up to $1.15 billion, extending its long-established epilepsy franchise into regenerative medicine and advanced therapies. Neurona’s lead asset, NRTX-1001, is a neuronal cell therapy being developed in Phase I/II trials for drug-resistant mesial temporal lobe epilepsy. Designed as a single-dose approach aimed at restoring […]

Medical Industry News

Gilead Sciences to Acquire Tubulis to Expand Its ADC Capabilities in Oncology

Gilead Sciences has announced an agreement to acquire Germany-based clinical-stage biotech Tubulis in a deal valued at up to $5 billion, expanding its oncology pipeline through next-generation antibody-drug conjugate, or ADC, technology. The acquisition adds Tubulis’ lead programme TUB-040, along with its proprietary Tubutecan linker-payload technology and broader ADC platform. The transaction also builds on […]

Gene Therapy

FDA Grants Accelerated Approval to Kresladi for Severe LAD-I

On March 27, the U.S. FDA approved Rocket Pharmaceuticals’ gene therapy Kresladi for severe Leukocyte Adhesion Deficiency-I (LAD-I). Kresladi is the first approved gene therapy for LAD-I. The decision marks an important step forward for gene therapy in ultra-rare diseases, where both clinical value and execution capability remain critical. Key points First approved gene therapy […]

Medical Industry News

Greenstaff Life Sciences at BIOCHINA2026

Last week, Greenstaff Life Sciences attended BIOCHINA2026 in Suzhou, China. Hiroshi Yamaguchi, Head of Greenstaff Life Sciences, and Summer Wang, Director of Greenstaff Medical China, attended the conference and engaged in discussions and exchanges across the life sciences community. Across the event, strong discussions took place around innovation, collaboration, and the future of biotech in […]

Medical Industry News

Japan Grants Conditional Approval for iPSC-Derived Regenerative Medicine Products

In March 2026, Japan’s Ministry of Health, Labour and Welfare (MHLW) granted conditional marketing authorization to two regenerative medicine products derived from induced pluripotent stem cells (iPSCs). The decision represents a significant milestone for the regenerative medicine sector, as these therapies could become the first iPSC-based treatments to receive regulatory approval globally. Since induced pluripotent […]

Medical Industry News

Gilead to Acquire CAR-T Developer Arcellx for $7.8 Billion

Gilead Sciences has entered into a definitive agreement to acquire Arcellx for approximately $7.8 billion, securing full ownership of its next-generation CAR-T program. Transaction & Development Overview Total deal value: approximately $7.8B (upfront plus contingent value rights) Lead asset: anitocabtagene autoleucel (anito-cel) BCMA-directed CAR-T therapy Target indication: relapsed/refractory multiple myeloma Clinical studies indicate deep and […]

Gene Therapy

Australia’s First SLE Patient Achieves Remission with CAR-T Cell Therapy

Monash University / Monash Health have announced that a patient with systemic lupus erythematosus (SLE) has achieved remission following treatment with CAR-T cell therapy.This represents the first clinical application of CAR-T therapy for an autoimmune disease in Australia, extending a modality long established in haematological oncology into a new therapeutic area. CAR-T cell therapy involves […]